Drugs Approved for Childhood Cancers
This page lists cancer drugs approved by the Food and Drug Administration (FDA) for use in children. The list includes generic and brand names. The drug names link to NCI’s Cancer Drug Information summaries. There are drugs and drug combinations used to treat children with cancer that are not listed here.
Drugs Approved for Acute Lymphoblastic Leukemia (ALL)
- Asparaginase Erwinia Chrysanthemi (Erwinaze)
- Asparaginase Erwinia Chrysanthemi (Recombinant)-rywn (Rylaze)
- Blinatumomab (Blincyto)
- Calaspargase Pegol-mknl (Asparlas)
- Clofarabine (Clolar)
- Cyclophosphamide
- Cytarabine
- Dasatinib (Sprycel)
- Daunorubicin Hydrochloride
- Imatinib Mesylate (Gleevec, Imkeldi)
- Mercaptopurine (Purinethol, Purixan)
- Methotrexate Sodium (Trexall, Xatmep)
- Nelarabine (Arranon)
- Pegaspargase (Oncaspar)
- Revumenib Citrate (Revuforj)
- Rituximab (Rituxan)
- Tisagenlecleucel (Kymriah)
- Vincristine Sulfate
Drugs Approved for Acute Myeloid Leukemia (AML)
- Gemtuzumab Ozogamicin (Mylotarg)
- Revumenib Citrate (Revuforj)
- Treosulfan (Grafapex)
- Vincristine Sulfate
Drugs Approved for Blastic Plasmacytoid Dendritic Cell Neoplasm
Drugs Approved for Chronic Myelogenous Leukemia (CML)
- Bosutinib (Bosulif)
- Cytarabine
- Dasatinib (Sprycel)
- Imatinib Mesylate (Gleevec, Imkeldi)
- Nilotinib (Tasigna)
Drugs Approved for Juvenile Myelomonocytic Leukemia (JMML)
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